Gene therapy achieves benefits in rare pediatric disease
Gene therapy has emerged as one of the greatest hopes for the treatment of rare diseases, including cerebral adrenoleukodystrophy (CALD). ...
Gene therapy has emerged as one of the greatest hopes for the treatment of rare diseases, including cerebral adrenoleukodystrophy (CALD). ...
Since 1979, the Region of Murcia has been carrying out the Neonatal Screening Program, the largest in Spain, which is ...